First FDA-approved gene therapy for children with severe LAD-I due to biallelic variants in ITGB2. S...
Rocket Pharmaceuticals Announces FDA Approval of KRESLADI™ for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I)
First FDA-approved gene therapy for children with severe LAD-I due to biallelic variants in ITGB2. Severe LAD-I is an ultra-rare, life-threatening pediatric...
Author: Business Wire
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